Funded Research Projects

2009

Analysis of mRNA transport and local protein syntheses in axons of SMA motor neurons

Principal investigator(s):

Dr. Claudia Fallini

2009

Antisense oligomer induced restoration of expression as a therapy for Spinal Muscular Atrophy

Principal investigator(s):

Dr. Steve Wilton

2009

Evaluation of new AAV-mediated gene therapy strategies in a feline model of Spinal Muscular Atrophy

Principal investigator(s):

Dr. Béatrice Joussemet

2009

Gene therapy for Spinal Muscular Atrophy by a correction of SMN2 MRNA splicing

Principal investigator(s):

Dr. Rachel Nlend Nlend

2009

Invastigating the temporal requirements of the SMN protein in Spinal Muscular Atrophy

Principal investigator(s):

Dr. Umrao Monani

2009

PTEN modulation effects on motor neuron axonal growth and neuromuscular junction size in Spinal Muscular Atrophy

Principal investigator(s):

Professor Mimoun Azzouz

2009

The S. pombe model organism: tool to find suppressors of snRNP-mediated splicing defects”

Principal investigator(s):

Dr. Remy Bordonné

2008

A two-pronged approach to develop a treatment for Spinal Muscular Atrophy

Principal investigator(s):

Dr. Monir Shababi